| All, # (%) 50 subjects | CTP A, # (%) 15 subjects | CTP B, # (%) 24 subjects | CTP C, # (%) 11 subjects | P value |
---|---|---|---|---|---|
Female | 35 (70.0) | 11 (73.3) | 16 (66.7) | 8 (72.7) | NS |
Caucasian | 46 (92.0) | 13 (86.7) | 23 (95.8) | 10 (90.9) | NS |
Age of onset  Median (IQR) | 9.62 (6.3, 11.6) | 9.30 (6.9, 11.9) | 9.27 (4.8, 10.5) | 10.3 (5.7, 13.4) | NS |
Age at study entry  Median (IQR) | 13 (9.8, 14.5) | 13.2 (9.8, 14.1) | 11.9 (6.8, 15.2) | 13.3 (11.2, 14.3) | NS |
Subtype: | Â | Â | Â | Â | 0.011 |
 Circumscribed superficial | 4 (8.0) | 0 | 1 (4.2) | 3 (27.3) | |
 Circumscribed deep | 3 ( 6.0) | 0 | 0 | 3 (27.3) | |
 Linear head | 12 (24.0) | 3 (20.0) | 6 (25.0) | 3 (27.3) | |
 Linear trunk/limb | 18 (36.0) | 8 (53.3) | 9 (37.5) | 1 (9.1) | |
 Generalized | 5 (10.0) | 2 (13.3) | 3 (12.5) | 0 | |
 Pansclerotic | 1 (2.0) | 0 | 1 (4.2) | 0 | |
 Mixed | 6 (12.0) | 2 (13.3) | 4 (16.7) | 0 | |
Anatomic Location | Â | Â | Â | Â | Â |
 Head | 20 (40.0) | 4 (26.7) | 11 (45.8) | 5 (45.5) | NS |
 Trunk | 23 (46.0) | 7 (46.7) | 11 (45.8) | 5 (45.5) | NS |
 Limb | 29 (58.0) | 11 (73.3) | 15 (62.5) | 3 (27.3) | 0.052 |
Prior Systemic Treatment | 9 (18.0) | 2 (13.3) | 7 (29.2) | 0 | 0.097 |
ANA positivity | 23 (54.8) | 5 (41.7) | 15 (79.0) | 3 (27.3) | 0.013 |
Extracutaneous morbidity | 37 (74.0) | 11 (73.3) | 18 (75.0) | 8 (72.7) | NS |
Deviation from CTP | 24 (48.0) | 8 (53.3) | 11 (45.8) | 5 (45.5) | NS |
MD Activity status at 12 months vs baseline | Â | Â | Â | Â | NS |
 Major improvement | 22 (50.0) | 4 (33.3) | 13 (56.5) | 5 (55.5) | |
 Moderate improvement | 15 (34.1) | 6 (50.0) | 7 (30.4) | 2 (22.2) | |
 Mild improvement | 6 (13.6) | 2 (16.7) | 2 (8.7) | 2 (22.2) | |
 Mild worsening | 1 (2.3) | 0 | 1 (4.4) | 0 | |
Inadequate response to CTP | 13 (26.0) | 4 (33.3) | 8 (33.3) | 1 (9.1) | NS |
Any Adverse Event | 33 (66.0) | 7 (46.7) | 17 (70.8) | 9 (81.8) | NS |
AE grade 1 | 26 (52.0) | 6 (40.0) | 11 (45.8) | 9 (81.8) | NS |
AE grade 2 | 22 (44.0) | 4 (26.7) | 14 (58.3) | 4 (36.4) | NS |
AE Grade 3 | 1 (2.3) | 0 | 1 (4.4) | 0 | NS |